The entry into the clinic of CFTR modulators such as TRIKAFTA has significantly improved life for ∼90% CF patients carrying one or two F508del mutations but challenges remain for rare CFTR mutations and the management of lung infections @SaraOcana1 https://bit.ly/3aRafQF.

The era of CFTR modulators: improvements made and remaining challenges

Laselva, Onofrio;
2020-01-01

Abstract

The entry into the clinic of CFTR modulators such as TRIKAFTA has significantly improved life for ∼90% CF patients carrying one or two F508del mutations but challenges remain for rare CFTR mutations and the management of lung infections @SaraOcana1 https://bit.ly/3aRafQF.
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Utilizza questo identificativo per citare o creare un link a questo documento: https://hdl.handle.net/11369/392262
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